BioNews
Vector
A delivery system used in the laboratory to carry foreign DNA into a cell. Modified viruses are commonly used as vectors in gene therapy.
Personalised cancer treatment uses genome-edited T cells
A personalised form of genome-edited T cell therapy has shown promising results for the treatment of solid tumours...
Gene therapy partly restores colour perception in completely colour blind children
Gene therapy has partly restored colour detection in two children that were born totally colour blind...
Haemophilia B gene therapy reduces risk of bleeding
A new method of gene therapy has shown initial success in treating patients with the bleeding disorder haemophilia B...
Five-month-old baby receives £1.8 million gene therapy on the NHS
A baby has become the first NHS patient to receive gene therapy for spinal muscular atrophy...
Spinal muscular atrophy gene therapy coming to the NHS
The NHS has agreed a deal to make gene therapy available for children with spinal muscular atrophy...
Base editing offers hope for child ageing disease
A type of genome editing had been used in mice to treat the symptoms of progeria, a fatal premature ageing disease in children...
Monkey HIV cut from host DNA by CRISPR
CRISPR-based genome editing has been used to remove an HIV-like virus from monkey DNA, bringing researchers a step closer to developing an HIV cure...
Retinal gene therapy trial shows positive result
A clinical trial using gene therapy for treating a common cause of genetic blindness published positive results in Nature Medicine...
New FDA guidelines for gene therapy products
The US Food and Drug Administration has released seven new guidelines that will help scientists safely develop novel gene therapy products...