BioNews
CRISPR therapy treats rare genetic inflammatory disorder
A single dose of a CRISPR-based gene therapy could cure inflammation in people affected by a rare condition that causes life-threatening swelling attacks, according to a new clinical trial...
Two gene therapies show promise in treating rare genetic deafness
Two clinical studies, trialing different gene therapies, have improved the hearing of children with a rare form of congenital deafness...
Gene therapy significantly reduces seizures in epilepsy mouse model
A new gene therapy has been successfully tested in mice that could provide an alternative to surgery in children with drug resistant epilepsy...
Podcast Review: How Gene Therapy is Offering Hope – Once Again
The past, present and future of gene therapies is discussed in this Pulse podcast...
Two gene therapies for sickle cell disease approved by FDA
Two gene therapies for the treatment of sickle cell disease have been approved by the US Food and Drug Administration...